Making a Difference – The Business of Rare Disease Drug Development
Drug development designed to treat rare disease is both a noble cause and a risky business. Rare diseases are typically deadly, debilitating, and devastating for…
Rare Diseases
Defying the Odds: Speeding Patient Access to Life-Changing Treatments in Rare Disease
To deliver treatments for rare diseases more quickly, companies share how they are adapting their launch strategies and engaging more deeply with physicians and experts….
How AI Helps Diagnose Rare Diseases
Rare diseases pose a significant challenge for health care professionals. These conditions — often complex and elusive — lead patients through a lengthy journey before…
Patients Are Waiting: Speeding Time to Treatment in Rare Disease
Companies are overcoming challenges to develop, launch, and educate on new rare disease medicines and treatment faster. Rare diseases are no longer rare. Every year,…
The Emotional Odyssey of a Rare Disease Diagnosis: Digging Deeper, To Do Better
Approximately 6% of the population is affected by a rare disease diagnosis, meaning that collectively it is not so rare at all. While the 7,000…
A Digital Education Revolution for People Living with Rare Disease
As we approach Rare Disease Day on 28 February, it puts into perspective the estimated 300 million people across the globe living with a rare…
Patient-data Platform Raremark Raises £3m to Enable Precision Medicine in Rare Disease
Raremark has raised £3m in funding from investors, led by AlbionVC and Ananda Ventures, with participation from Oltre Venture and from existing major investor the…